Doctors Used first Personalized Gene-editing Therapy on Baby
A team of doctors and scientists has successfully treated a rare genetic disorder using the first personalized gene-editing therapy. The results, published in The New England Journal of Medicine, were accompanied by an editorial from a former FDA gene-therapy regulator. The patient in this landmark case was KJ, an infant diagnosed with CPS1 deficiency—a condition […]
Doctors Used first Personalized Gene-editing Therapy on Baby Read More »









